Exploring Fabry Disease Treatment Options
HealthFabry disease treatment options have advanced significantly, offering several options to reduce symptoms and slow disease progression. The primary therapies include Galafold (migalastat), enzyme replacement therapy (ERT), pain management medications and targeted lifestyle adjustments. Each treatment targets different aspects of Fabry pathology, aiming to restore enzyme function, minimize tissue damage and improve daily well-being. Galafold is the first approved oral pharmacological chaperone for Fabry disease. It selectively binds and stabilizes certain mutant forms of the α-galactosidase A enzyme, enhancing its...